Epilepsy affects more than 50 million people worldwide, making it one of the most common neurological disorders. Although ...

Scientists at the MRC Laboratory of Medical Sciences (LMS) have discovered a DNA-based “dimmer switch” that regulates the activity of a critical developmental gene, Cdx2. This work could pave the way ...

A new study describes a gene therapy strategy that uses the brain's own glymphatic transport system to distribute engineered viral vectors throughout the brain.

The evolution of biomedical science can be appreciated through studies of hemoglobin, the oxygen-carrying protein in red cells. Before molecular cloning, the geneticist Arno Motulsky noted, “Many ...

Professor Hirohide Saito (Department of Life Science Frontiers at CiRA / The University of Tokyo) and Assistant Professor Hirohisa Ohno (Department of Life Science Frontiers at CiRA) recently led a ...

HOUSTON and MIAMI, SEPTEMBER 5, 2025 ― The University of Texas MD Anderson Cancer Center and Phoenix SENOLYTIX, Inc., today announced a global cross-licensing agreement to facilitate work that will ...

A single infusion of a CRISPR-based gene therapy eliminated painful crises in 27 of 28 patients with severe sickle cell ...

Gene silencing refers to any mechanism that turns down or switches off the expression of a specific gene so that less of its protein, or none at all, is produced. Crucially, the gene's DNA is left ...

Persistence Market Research, a leading management consulting firm, has released this update on the gene editing market. Gene ...

Recent data published in NEJM demonstrates that CRISPR gene-editing therapy achieves complete clinical efficacy endpoints in ...