After decades of advocacy work, columnist Patrick Moeschen is glad to see MD patients treated as experts given their lived ...

The FDA is reviewing full approval bids for the Duchenne therapies Amondys 45 and Vyondys 53, with decisions expected by ...

A CITGO golf fundraiser in Louisiana raised a record $756,800 for MDA to support people living with neuromuscular diseases ...

MDA criticized a DOJ memorandum on disability care, saying it threatens in-home and community-based services for people with ...

I have heard that said hundreds of times over the past 25 years, and I hated hearing it. I always had a response ready: “Sure, but my heart is fuller,” I would say. However, I’m currently in a season ...

Brenda Song, MD, is a neurologist who directs the UMass Duchenne Muscular Dystrophy Program, and she is a pioneer in organizing multidisciplinary care for Duchenne populations. She explains how ...

On July 29, Capricor Therapeutics will meet with an FDA advisory committee regarding its second attempt to win deramiocel's approval for DMD.

Columnist Betty Vertin has been worried about weight gain and her stress levels, but the results of her annual physical were good news.

Being part of the PPMD conference's Adult Advisory Committee has helped columnist Patrick Moeschen bond with those who share his diagnosis.

Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.