The one-time gene therapy Itvisma will now be available for people with SMA of all ages in the European Union after winning ...

Columnist Kevin Schaefer says that the days of having a hospital room as a place of residency are hopefully behind him, which ...

While attending concerts, columnist Connie Chandler was frustrated that she was unable to express joy. Then she found a clap ...

Columnist Helen Baldwin says she learned this lesson when her third baby, Jeffrey, was born with SMA in the late 1990s.

SMA Europe is accepting proposals for research projects, with motor regeneration and SMA metabolism among the priority areas ...

Restoring SNAP23 or replenishing these vesicles shows promise for improving bone health in SMA. Weak bones in people with ...

Omaveloxolone (approved for Friedreich's ataxia) may help protect cells from stress and correct underlying dysfunction in SMA ...

A study found Evrysdi (risdiplam) helps the body produce more SMN, and also revealed genetic differences between SMA types 2 and 3.

For guest writer Maria Llave, having consistent access to Medicaid provides peace of mind, enabling her to focus on her future.

Columnist Brianna Albers says that moving out of her long-time home with SMA has turned out to be her biggest gamble yet.

Treatment with Zolgensma helped children with SMA gain or maintain motor milestones and motor function, a real-world study in ...

My caregiver held the toothpaste tube in both hands, meticulously squishing it flat from the bottom all the way up to the nozzle. I laughed: “It’s OK, I have a whole new tube ready to go in the closet ...