After decades of advocacy work, columnist Patrick Moeschen is glad to see MD patients treated as experts given their lived ...

I have heard that said hundreds of times over the past 25 years, and I hated hearing it. I always had a response ready: “Sure, but my heart is fuller,” I would say. However, I’m currently in a season ...

The FDA is reviewing full approval bids for the Duchenne therapies Amondys 45 and Vyondys 53, with decisions expected by ...

On July 29, Capricor Therapeutics will meet with an FDA advisory committee regarding its second attempt to win deramiocel's approval for DMD.