ARPA-H gene editing program THRIVE awards $160 million to seven research teams tasked with building scalable base-editing ...
A new study describes a gene therapy strategy that uses the brain's own glymphatic transport system to distribute engineered ...
Novartis already received FDA approval of ITVISMA as a gene therapy for the treatment of patients with SMA. Read why NVS ...
A new study describes a gene therapy strategy that uses the brain's own glymphatic transport system to distribute engineered viral vectors throughout the brain.