The Lancet

Patient profiles and early response in patients with systemic lupus erythematosus initiating anifrolumab: interim analysis from the ongoing multicentre observational REVEAL study

dRheumatology Unit, Department of Medicine, University of Padua, Padua, Italy eDivision of Rheumatology, Department of Internal Medicine and Therapeutics, University of Pavia and Division of ...
The Lancet

Safety and efficacy of intravenous onasemnogene abeparvovec gene therapy in patients with spinal muscular atrophy type 1: interim analysis from LT-001, a long-term follow-up ...

aCenter for Gene Therapy, Nationwide Children's Hospital, 700 Children's Dr, Columbus, OH, 43205, USA bThe Ohio State University College of Medicine, 700 Children's Dr, Columbus, OH, 43205, USA ...